A direct gene transfer strategy via brain internal capsule reverses the biochemical defect in Tay-Sachs disease (Q29395388)
scientific article (publication date: 16 June 2005)
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(P1476) "A direct gene transfer strategy via brain internal capsule reverses the biochemical defect in Tay-Sachs disease" (language: en)
(P2093) M G Cusella De Angelis
G Bregola
K Sandhoff
C Bordignon
A Orlacchio
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description scientific article (publication date: 16 June 2005)

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